Ultra-Rare Gene-based Therapy (URGenT) Network Resource Access (X01, Clinical Trial Not Allowed)

The purpose of this Notice of Funding Opportunity (NOFO) is to provide investigators with a mechanism to access contract research/medical organizations (CROs/CMOs) and subject matter experts (SMEs) within the NINDS Ultra-Rare Gene-based Therapy (URGenT) Network to support planning, manufacturing, and limited nonclinical therapeutic development efforts. * The opportunity is for access to resources, not a direct funding opportunity. * The URGenT Network aims to support the development of gene-based therapies for ultra-rare diseases. * Eligible applicants include various types of organizations, such as state governments, nonprofits, and for-profit companies. * The opportunity is open for a period of approximately 3 years, with a closing date of January 31, 2028.